Agalsidase alfa: specific treatment for Fabry disease
- PMID: 12096664
- DOI: 10.12968/hosp.2002.63.6.2005
Agalsidase alfa: specific treatment for Fabry disease
Abstract
Fabry disease is a rare genetic lysosomal storage disorder characterized by a deficiency of the enzyme alpha-galactosidase A. The recent availability of enzyme-replacement therapy with agalsidase alfa offers specific treatment for this serious, progressive condition.
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