Duchenne muscular dystrophy and dystrophin: pathogenesis and opportunities for treatment
- PMID: 15470384
- PMCID: PMC1299132
- DOI: 10.1038/sj.embor.7400221
Duchenne muscular dystrophy and dystrophin: pathogenesis and opportunities for treatment
Abstract
Third in Molecular Medicine Review Series
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References
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- Barresi R et al. (2004) LARGE can functionally bypass α-dystroglycan glycosylation defects in distinct congenital muscular dystrophies. Nat Med 10: 696–703 - PubMed
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