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Review
. 2005 Oct 29;331(7523):1016-9.
doi: 10.1136/bmj.331.7523.1016.

Orphan drugs and the NHS: should we value rarity?

Christopher McCabe  1 , Karl Claxton, Aki Tsuchiya
Affiliations
Review

Orphan drugs and the NHS: should we value rarity?

Christopher McCabe et al. BMJ. .

Abstract

The growing number and costs of drugs for rare diseases are straining healthcare budgets. Decisions on funding these treatments need to be made on a sound basis

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Figures

Figure 1
Figure 1
Special status for drugs for rare diseases such as neurofibromatosis may be unsustainable Credit: PENNY TWEEDIE/SPL
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References

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