Preliminary results of gene therapy for retinal degeneration
- PMID: 18441372
- DOI: 10.1056/NEJMe0803081
Preliminary results of gene therapy for retinal degeneration
Comment on
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Safety and efficacy of gene transfer for Leber's congenital amaurosis.N Engl J Med. 2008 May 22;358(21):2240-8. doi: 10.1056/NEJMoa0802315. Epub 2008 Apr 27. N Engl J Med. 2008. PMID: 18441370 Free PMC article. Clinical Trial.
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Effect of gene therapy on visual function in Leber's congenital amaurosis.N Engl J Med. 2008 May 22;358(21):2231-9. doi: 10.1056/NEJMoa0802268. Epub 2008 Apr 27. N Engl J Med. 2008. PMID: 18441371 Clinical Trial.
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