Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; report of three expert workshops: TREAT-NMD/ENMC workshop on outcome measures, 12th--13th May 2007, Naarden, The Netherlands; TREAT-NMD workshop on outcome measures in experimental trials for DMD, 30th June--1st July 2007, Naarden, The Netherlands; conjoint Institute of Myology TREAT-NMD meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France

E Mercuri¹, A Mayhew, F Muntoni, S Messina, V Straub, G J Van Ommen, T Voit, E Bertini, K Bushby; TREAT-NMD Neuromuscular Network

Collaborators, Affiliations

Collaborators

TREAT-NMD Neuromuscular Network:
E Mercuri, A Ambrosini, C Beràrd, E Bertini, K Bushby, J Cobben, M Eagle, J Florence, A Glanzmann, L S Hynan, M Main, A Mayhew, E Mazzone, S Messina, F Muntoni, S Rudnik-Schoeneborn, B Steffensen, K Swoboda, M de Visser, T Voit, R Griggs, A Ambrosini, L Atkinson, J Christensen, G Cossu, V Cwik, K Davies, S Del Signore, P Denefle, M Denti, G Elfring, D Escolar, K Flanigan, P Furlong, E Heslop, S de Kimpe, R Korinthenberg, H Laouenan, S Lynn, J Marler, T Meier, F Muntoni, G J van Ommen, T Partridge, J Porter, G Spinella, S Takeda, S Tapscott, J Tinsley, Y Torrente, J Tremblay, E Venneker, J Verschuuren, J Scott, V Straub, A Urtizberea, E Vroom, D Wells, B Wong, T Voit, K Aminian, M Eagle, J Florence, Y P Jeannet, M Main, A Mayhew, E Mazzone, E Mercuri, S Messina, F Muntoni

Affiliation

¹ Department of Paediatric Neurology, Catholic University, Rome, Italy. mercuri@rm.unicatt.it

PMID: 18818076
DOI: 10.1016/j.nmd.2008.07.003

Towards harmonisation of outcome measures for DMD and SMA within TREAT-NMD; report of three expert workshops: TREAT-NMD/ENMC workshop on outcome measures, 12th--13th May 2007, Naarden, The Netherlands; TREAT-NMD workshop on outcome measures in experimental trials for DMD, 30th June--1st July 2007, Naarden, The Netherlands; conjoint Institute of Myology TREAT-NMD meeting on physical activity monitoring in neuromuscular disorders, 11th July 2007, Paris, France

E Mercuri et al. Neuromuscul Disord. 2008 Nov.

. 2008 Nov;18(11):894-903.

doi: 10.1016/j.nmd.2008.07.003. Epub 2008 Sep 24.

Authors

E Mercuri¹, A Mayhew, F Muntoni, S Messina, V Straub, G J Van Ommen, T Voit, E Bertini, K Bushby; TREAT-NMD Neuromuscular Network

Collaborators

TREAT-NMD Neuromuscular Network:
E Mercuri, A Ambrosini, C Beràrd, E Bertini, K Bushby, J Cobben, M Eagle, J Florence, A Glanzmann, L S Hynan, M Main, A Mayhew, E Mazzone, S Messina, F Muntoni, S Rudnik-Schoeneborn, B Steffensen, K Swoboda, M de Visser, T Voit, R Griggs, A Ambrosini, L Atkinson, J Christensen, G Cossu, V Cwik, K Davies, S Del Signore, P Denefle, M Denti, G Elfring, D Escolar, K Flanigan, P Furlong, E Heslop, S de Kimpe, R Korinthenberg, H Laouenan, S Lynn, J Marler, T Meier, F Muntoni, G J van Ommen, T Partridge, J Porter, G Spinella, S Takeda, S Tapscott, J Tinsley, Y Torrente, J Tremblay, E Venneker, J Verschuuren, J Scott, V Straub, A Urtizberea, E Vroom, D Wells, B Wong, T Voit, K Aminian, M Eagle, J Florence, Y P Jeannet, M Main, A Mayhew, E Mazzone, E Mercuri, S Messina, F Muntoni

Affiliation

¹ Department of Paediatric Neurology, Catholic University, Rome, Italy. mercuri@rm.unicatt.it

PMID: 18818076
DOI: 10.1016/j.nmd.2008.07.003

No abstract available

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Comment in

Outcome measures in Duchenne muscular dystrophy: are we ready for the new therapeutic era?
Merkies IS, Faber CG. Merkies IS, et al. Neuromuscul Disord. 2009 Jun;19(6):447. doi: 10.1016/j.nmd.2009.04.005. Epub 2009 May 30. Neuromuscul Disord. 2009. PMID: 19482474 No abstract available.

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Mercuri E, McDonald C, Mayhew A, Florence J, Mazzone E, Bianco F, Decostre V, Servais L, Ricotti V, Goemans N, Vroom E. Mercuri E, et al. Neuromuscul Disord. 2012 Nov;22(11):1025-8. doi: 10.1016/j.nmd.2012.06.006. Epub 2012 Jul 13. Neuromuscul Disord. 2012. PMID: 22795657 Free PMC article. No abstract available.

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