Case Reports
doi: 10.1016/j.jpeds.2008.11.031.
Homozygous alpha-thalassemia treated with intrauterine transfusions and unrelated donor hematopoietic cell transplantation
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- PMID: 19364562
- DOI: 10.1016/j.jpeds.2008.11.031
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Case Reports
Homozygous alpha-thalassemia treated with intrauterine transfusions and unrelated donor hematopoietic cell transplantation
J Pediatr.
2009 May.
Abstract
Recently, intrauterine transfusions and hematopoietic cell transplantation (HCT) have changed homozygous alpha-thalassemia from a frequently fatal disease to a potentially survivable condition. We present a patient with Hemoglobin Bart's disease who was cured after failing to engraft with 1 unrelated HCT, but engrafting after a second unrelated donor HCT.
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