PTC124 for cystic fibrosis
- PMID: 19394530
- DOI: 10.1016/S0140-6736(09)60819-9
PTC124 for cystic fibrosis
Comment on
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Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial.Lancet. 2008 Aug 30;372(9640):719-27. doi: 10.1016/S0140-6736(08)61168-X. Epub 2008 Aug 20. Lancet. 2008. PMID: 18722008 Clinical Trial.
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