Enzyme-replacement therapy for Gaucher's disease
- PMID: 1944489
- DOI: 10.1056/NEJM199112193252513
Enzyme-replacement therapy for Gaucher's disease
Comment on
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Replacement therapy for inherited enzyme deficiency--macrophage-targeted glucocerebrosidase for Gaucher's disease.N Engl J Med. 1991 May 23;324(21):1464-70. doi: 10.1056/NEJM199105233242104. N Engl J Med. 1991. PMID: 2023606 Clinical Trial.
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