Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation
Review
. 1990 Jun;4(3):589-602.

Bone marrow transplantation for genetic diseases

C Lenarsky  1 , D B Kohn, K I Weinberg, R Parkman
Affiliations
  • PMID: 2113518
Review

Bone marrow transplantation for genetic diseases

C Lenarsky et al. Hematol Oncol Clin North Am. 1990 Jun.

Abstract

Bone marrow transplantation is the treatment of choice for a number of genetic diseases. Recently, bone marrow transplantation has been increasingly used for erythroid disorders, such as thalassemia and sickle cell anemia. A number of inherited metabolic disorders (i.e., storage diseases, leukodystrophies, and the like) may be corrected with a marrow transplant. Successful correction of genetic diseases with allogeneic bone marrow transplantation lays the groundwork for the use of specific gene therapy.

PubMed Disclaimer

MeSH terms