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. 2011 Feb;29(2):121-8.
doi: 10.1038/nbt.1769.

Gene therapy finds its niche

Cormac Sheridan

Gene therapy finds its niche

Cormac Sheridan. Nat Biotechnol. 2011 Feb.

Erratum in

  • Nat Biotechnol. 2011 May;29(5):459

Abstract

Gene therapy is finally poised to make a contribution to the treatment of debilitating, highly penetrant genetic diseases that have proved intractable to other regimens.

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