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Editorial
. 2011 Apr 28;364(17):1670-1.
doi: 10.1056/NEJMe1102290. Epub 2011 Mar 16.

Patient organizations and research on rare diseases

Julie R Ingelfinger, Jeffrey M Drazen
Editorial

Patient organizations and research on rare diseases

Julie R Ingelfinger et al. N Engl J Med. .
No abstract available

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  • Efficacy and safety of sirolimus in lymphangioleiomyomatosis.
    McCormack FX, Inoue Y, Moss J, Singer LG, Strange C, Nakata K, Barker AF, Chapman JT, Brantly ML, Stocks JM, Brown KK, Lynch JP 3rd, Goldberg HJ, Young LR, Kinder BW, Downey GP, Sullivan EJ, Colby TV, McKay RT, Cohen MM, Korbee L, Taveira-DaSilva AM, Lee HS, Krischer JP, Trapnell BC; National Institutes of Health Rare Lung Diseases Consortium; MILES Trial Group. McCormack FX, et al. N Engl J Med. 2011 Apr 28;364(17):1595-606. doi: 10.1056/NEJMoa1100391. Epub 2011 Mar 16. N Engl J Med. 2011. PMID: 21410393 Free PMC article. Clinical Trial.

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