Antisense therapeutics: Systemic reawakening of a silent gene to improve survival in SMA
- PMID: 22129985
- DOI: 10.1038/nrd3608
Antisense therapeutics: Systemic reawakening of a silent gene to improve survival in SMA
Comment on
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Peripheral SMN restoration is essential for long-term rescue of a severe spinal muscular atrophy mouse model.Nature. 2011 Oct 5;478(7367):123-6. doi: 10.1038/nature10485. Nature. 2011. PMID: 21979052 Free PMC article.
References
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- Nature. 2011 Oct 05;478(7367):123-6 - PubMed
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