Comment on

• Gene therapy for retinitis pigmentosa caused by MFRP mutations: human phenotype and preliminary proof of concept.

  Dinculescu A, Estreicher J, Zenteno JC, Aleman TS, Schwartz SB, Huang WC, Roman AJ, Sumaroka A, Li Q, Deng WT, Min SH, Chiodo VA, Neeley A, Liu X, Shu X, Matias-Florentino M, Buentello-Volante B, Boye SL, Cideciyan AV, Hauswirth WW, Jacobson SG. Dinculescu A, et al. Hum Gene Ther. 2012 Apr;23(4):367-76. doi: 10.1089/hum.2011.169. Epub 2012 Jan 26. Hum Gene Ther. 2012. PMID: 22142163 Free PMC article.
• Long-term rescue of retinal structure and function by rhodopsin RNA replacement with a single adeno-associated viral vector in P23H RHO transgenic mice.

  Mao H, Gorbatyuk MS, Rossmiller B, Hauswirth WW, Lewin AS. Mao H, et al. Hum Gene Ther. 2012 Apr;23(4):356-66. doi: 10.1089/hum.2011.213. Epub 2012 Mar 28. Hum Gene Ther. 2012. PMID: 22289036 Free PMC article.
• Dextran and protamine-based solid lipid nanoparticles as potential vectors for the treatment of X-linked juvenile retinoschisis.

  Delgado D, del Pozo-Rodríguez A, Solinís MÁ, Avilés-Triqueros M, Weber BH, Fernández E, Gascón AR. Delgado D, et al. Hum Gene Ther. 2012 Apr;23(4):345-55. doi: 10.1089/hum.2011.115. Epub 2012 Mar 29. Hum Gene Ther. 2012. PMID: 22295905