Gene delivery improvement for treating the lysosomal storage disorder metachromatic leukodystrophy
- PMID: 22900577
- DOI: 10.1089/hum.2012.2516
Gene delivery improvement for treating the lysosomal storage disorder metachromatic leukodystrophy
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Correction of brain oligodendrocytes by AAVrh.10 intracerebral gene therapy in metachromatic leukodystrophy mice.Hum Gene Ther. 2012 Aug;23(8):903-14. doi: 10.1089/hum.2012.015. Epub 2012 Jul 23. Hum Gene Ther. 2012. PMID: 22642214 Free PMC article.
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