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Editorial
. 2012 Oct 3;308(13):1377-8.
doi: 10.1001/jama.2012.12906.

Mexiletine for treatment of myotonia: a trial triumph for rare disease networks

Eric P Hoffman, Henry J Kaminski
Editorial

Mexiletine for treatment of myotonia: a trial triumph for rare disease networks

Eric P Hoffman et al. JAMA. .
No abstract available

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Conflict of interest statement

Conflict of Interest Disclosures: The authors have completed and submitted the ICMJE Form for Disclosure of Potential Conflicts of Interest. Dr Hoffman reported serving as a board member, holding founder shares in, and owning stock in Revera-Gen Biopharma; receiving royalties on a patent from Boston Children's Hospital; and receiving grants from the National Institutes of Health, Muscular Dystrophy Association, and the Foundation to Eradicate Duchenne. Dr Kaminski reported receiving fees from legal firms for expert testimony; and receiving grants from the National Institutes of Health and MG Foundation of America.

Comment on

References

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    1. Matthews E, Fialho D, Tan SV, et al. CINCH Investigators The non-dystrophic myotonias: molecular pathogenesis, diagnosis and treatment. Brain. 2010;133(Pt1):9–22. - PMC - PubMed
    1. Aban IB, Wolfe Gl, Cutter GR, et al. Mgtx Advisory Committee The MGTX experience: challenges in planning and executing an international, multicenter clinical trial. J Neuroimmunol. 2008:201–202. 80–84. - PMC - PubMed

Supplementary concepts