Transplantation of gene-corrected motor neurons as a therapeutic strategy for spinal muscular atrophy
- PMID: 23449105
- PMCID: PMC3642289
- DOI: 10.1038/mt.2013.23
Transplantation of gene-corrected motor neurons as a therapeutic strategy for spinal muscular atrophy
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References
-
- Parekh-Olmedo H., and, Kmiec EB. Progress and prospects: targeted gene alteration (TGA) Gene Ther. 2007;14:1675–1680. - PubMed
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