Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation
Editorial
. 2013 Sep;8(5):527-9.
doi: 10.2217/rme.13.46.

Prospects for stem cell therapy in neuronal ceroid lipofuscinosis

Editorial

Prospects for stem cell therapy in neuronal ceroid lipofuscinosis

Michael C Kruer et al. Regen Med. 2013 Sep.
No abstract available

PubMed Disclaimer

References

    1. Kollmann K, Uusi-Rauva K, Scifo E, Tyynelä J, Jalanko A, Braulke T. Cell biology and function of neuronal ceroid lipofuscinosis-related proteins. Biochim Biophys Acta. 2013 doi:pii:S0925-4439(13)00033-1. [Epub ahead of print] - PubMed
    1. Selden NR, Al-Uzri A, Huhn SL, et al. Central nervous system stem cell transplantation for children with neuronal ceroid lipofuscinosis. J Neurosurg Pediatr. 2013 Apr 12; [Epub ahead of print] - PubMed
    1. Van Diggelen OP, Keulemans JL, Kleijer WJ, Thobois S, Tilikete C, Voznyi YV. Pre- and postnatal enzyme analysis for infantile, late infantile and adult neuronal ceroid lipofuscinosis (CLN1 and CLN2). Eur J Paediatr Neurol. 2001;5(Suppl A):189–92. - PubMed
    1. Phillips SN, Muzaffar N, Codlin S, et al. Characterizing pathogenic processes in Batten disease: use of small eukaryotic model systems. Biochim Biophys Acta. Oct. 2006;1762(10):906–19. - PubMed
    1. Vieira C, Lucena R. Use of Cyclodextrin in Two Brazilian Girls With Niemann-Pick Type C – Intrathecal Report. 2012 Michael, Marcia, and Christa Parseghian Scientific Conference for Niemann-Pick Type C Research. 2012 Jun 7-9th;

Publication types

LinkOut - more resources