Neuromuscular disorders: from diagnosis to translational research, drug development and clinical trials
- PMID: 24240286
- PMCID: PMC4008827
- DOI: 10.1097/MOP.0b013e328365de49
Neuromuscular disorders: from diagnosis to translational research, drug development and clinical trials
Abstract
Pediatric neuromuscular disorders are a heterogeneous group of conditions that form four distinct groupings: (1) motor neuron diseases, (2) neuropathies, (3) disorders of the neuromuscular junction, and (4) myopathies.
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