Optimizing treatments in rare diseases: will our evidence come from registry data?

Affiliations

¹ Serviço de Hematologia, Instituto Português de Oncologia de Lisboa, Francisco Gentil, Lisbon, Portugal. Electronic address: amalmeida@ipolisboa.min-saude.pt.

Editorial

Antonio M Almeida. Leuk Res. 2014 Apr.

. 2014 Apr;38(4):421-2.

doi: 10.1016/j.leukres.2014.01.015. Epub 2014 Feb 6.

¹ Serviço de Hematologia, Instituto Português de Oncologia de Lisboa, Francisco Gentil, Lisbon, Portugal. Electronic address: amalmeida@ipolisboa.min-saude.pt.

No abstract available

Comment on

Azacitidine in CMML: matched-pair analyses of daily-life patients reveal modest effects on clinical course and survival.
Pleyer L, Germing U, Sperr WR, Linkesch W, Burgstaller S, Stauder R, Girschikofsky M, Schreder M, Pfeilstocker M, Lang A, Sliwa T, Geissler D, Schlick K, Placher-Sorko G, Theiler G, Thaler J, Mitrovic M, Neureiter D, Valent P, Greil R. Pleyer L, et al. Leuk Res. 2014 Apr;38(4):475-83. doi: 10.1016/j.leukres.2014.01.006. Epub 2014 Jan 18. Leuk Res. 2014. PMID: 24522248