Rare diseases and effective treatments: are we delivering?

doi:10.1016/S0140-6736(15)60297-5

. 2015 Feb 28;385(9970):750-2.

doi: 10.1016/S0140-6736(15)60297-5.

Rare diseases and effective treatments: are we delivering?

Affiliations

¹ Istituto Toscano Tumori, Florence, Italy.
² Department of Endocrinology and Metabolism, Academic Medical Center, Amsterdam, the Netherlands.
³ University Department of Medicine, University of Cambridge, Cambridge, UK.
⁴ IRCCS Istituto di Ricerche Farmacologiche Mario Negri, 24126 Bergamo, Italy; Azienda Ospedaliera Papa Giovanni XXIII, Bergamo, Italy.
⁵ Division of Nephrology, The Hospital for Sick Children, Toronto, Canada.
⁶ European Platform for Patients' Organizations Science and Industry, Brussels, Belgium.
⁷ Amyloidosis Research and Treatment Center, Department of Molecular Medicine, University of Pavia, Italy.
⁸ Pediatric Nephrology Division, Heidelberg University Center for Pediatrics and Adolescent Medicine, Heidelberg, Germany.
⁹ KU Leuven Department of Pharmaceutical and Pharmacological Sciences, Leuven, Belgium.
¹⁰ AIFA Italian Medicine Agency, Rome, Italy.
¹¹ IRCCS Istituto di Ricerche Farmacologiche Mario Negri, 24126 Bergamo, Italy.
¹² IRCCS Istituto di Ricerche Farmacologiche Mario Negri, 24126 Bergamo, Italy. Electronic address: giuseppe.remuzzi@marionegri.it.

PMID: 25752159
DOI: 10.1016/S0140-6736(15)60297-5

Rare diseases and effective treatments: are we delivering?

Lucio Luzzatto et al. Lancet. 2015.

. 2015 Feb 28;385(9970):750-2.

doi: 10.1016/S0140-6736(15)60297-5.

Authors

Affiliations

¹ Istituto Toscano Tumori, Florence, Italy.
² Department of Endocrinology and Metabolism, Academic Medical Center, Amsterdam, the Netherlands.
³ University Department of Medicine, University of Cambridge, Cambridge, UK.
⁴ IRCCS Istituto di Ricerche Farmacologiche Mario Negri, 24126 Bergamo, Italy; Azienda Ospedaliera Papa Giovanni XXIII, Bergamo, Italy.
⁵ Division of Nephrology, The Hospital for Sick Children, Toronto, Canada.
⁶ European Platform for Patients' Organizations Science and Industry, Brussels, Belgium.
⁷ Amyloidosis Research and Treatment Center, Department of Molecular Medicine, University of Pavia, Italy.
⁸ Pediatric Nephrology Division, Heidelberg University Center for Pediatrics and Adolescent Medicine, Heidelberg, Germany.
⁹ KU Leuven Department of Pharmaceutical and Pharmacological Sciences, Leuven, Belgium.
¹⁰ AIFA Italian Medicine Agency, Rome, Italy.
¹¹ IRCCS Istituto di Ricerche Farmacologiche Mario Negri, 24126 Bergamo, Italy.
¹² IRCCS Istituto di Ricerche Farmacologiche Mario Negri, 24126 Bergamo, Italy. Electronic address: giuseppe.remuzzi@marionegri.it.

PMID: 25752159
DOI: 10.1016/S0140-6736(15)60297-5

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Rare diseases and effective treatments: are we delivering?

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Rare diseases and effective treatments: are we delivering?

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