Muscular dystrophy: New exon-skipping strategy rescues dystrophin
- PMID: 25829275
- DOI: 10.1038/nrd4587
Muscular dystrophy: New exon-skipping strategy rescues dystrophin
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Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers.Nat Med. 2015 Mar;21(3):270-5. doi: 10.1038/nm.3765. Epub 2015 Feb 2. Nat Med. 2015. PMID: 25642938
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Functional correction in mouse models of muscular dystrophy using exon-skipping tricyclo-DNA oligomers.Nat Med. 2015 Mar;21(3):270-5. doi: 10.1038/nm.3765. Epub 2015 Feb 2. Nat Med. 2015. PMID: 25642938
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References
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- Nat Med. 2015 Mar;21(3):270-5 - PubMed
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