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Editorial
. 2015 Sep 10;373(11):1071-3.
doi: 10.1056/NEJMe1509055.

Lysosomal Acid Lipase Deficiency--A New Therapy for a Genetic Lipid Disease

Daniel J Rader  1
Affiliations
Editorial

Lysosomal Acid Lipase Deficiency--A New Therapy for a Genetic Lipid Disease

Daniel J Rader. N Engl J Med. .
No abstract available

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  • A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency.
    Burton BK, Balwani M, Feillet F, Barić I, Burrow TA, Camarena Grande C, Coker M, Consuelo-Sánchez A, Deegan P, Di Rocco M, Enns GM, Erbe R, Ezgu F, Ficicioglu C, Furuya KN, Kane J, Laukaitis C, Mengel E, Neilan EG, Nightingale S, Peters H, Scarpa M, Schwab KO, Smolka V, Valayannopoulos V, Wood M, Goodman Z, Yang Y, Eckert S, Rojas-Caro S, Quinn AG. Burton BK, et al. N Engl J Med. 2015 Sep 10;373(11):1010-20. doi: 10.1056/NEJMoa1501365. N Engl J Med. 2015. PMID: 26352813 Clinical Trial.

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