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Comment
. 2015 Dec;26(12):783-5.
doi: 10.1089/hum.2015.29012.jmq. Epub 2015 Dec 4.

Philanthropy and Advocacy-Led Development of Gene Therapies and Drugs for Alpha-1 Antitrypsin Deficiency

Jean-Marc Quach  1 , Robert Campbell  1 , John Walsh  1
Affiliations
Comment

Philanthropy and Advocacy-Led Development of Gene Therapies and Drugs for Alpha-1 Antitrypsin Deficiency

Jean-Marc Quach et al. Hum Gene Ther. 2015 Dec.
No abstract available

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References

    1. de Serres FJ. Worldwide racial and ethnic distribution of α1-antitrypsin deficiency: summary of an analysis of published genetic epidemiologic surveys. Chest 2002;122:1818–1829 - PubMed
    1. Chapman KR, Burdon JG, Piitulainen E, et al. ; RAPID Trial Study Group. Intravenous augmentation treatment and lung density in severe α1 antitrypsin deficiency (RAPID): a randomised, double-blind, placebo-controlled trial. Lancet 2015;386:360–368 - PubMed

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