Movement disorders: Targeted RNA or BDNF gene transfer protects against frataxin deficiency
- PMID: 26915729
- DOI: 10.1038/nrneurol.2016.19
Movement disorders: Targeted RNA or BDNF gene transfer protects against frataxin deficiency
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Activating frataxin expression by repeat-targeted nucleic acids.Nat Commun. 2016 Feb 4;7:10606. doi: 10.1038/ncomms10606. Nat Commun. 2016. PMID: 26842135 Free PMC article.
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Gene Transfer of Brain-derived Neurotrophic Factor (BDNF) Prevents Neurodegeneration Triggered by FXN Deficiency.Mol Ther. 2016 May;24(5):877-89. doi: 10.1038/mt.2016.32. Epub 2016 Feb 5. Mol Ther. 2016. PMID: 26849417 Free PMC article.
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