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. 2016 Jun;27(2):57-61.
doi: 10.1089/humc.2016.29010.ind. Epub 2016 Jun 6.

Investor Outlook: Rising from the Ashes; GSK's European Approval of Strimvelis for ADA-SCID

Joshua Schimmer  1 , Steven Breazzano  1
Affiliations

Investor Outlook: Rising from the Ashes; GSK's European Approval of Strimvelis for ADA-SCID

Joshua Schimmer et al. Hum Gene Ther Clin Dev. 2016 Jun.

Abstract

GlaxoSmithKline's (GSK) and partner San Raffaele Telethon Institute for Gene Therapy's recent positive European approval for Strimvelis for treatment of severe combined immunodeficiency due to adenosine deaminase deficiency (ADA-SCID) represents the second EU-approved gene therapy and the first γ-retrovirus and first ex vivo gene therapy. In this article we discuss the significance and implications of this historic approval for the broader gene therapy field.

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