Challenges ahead for trials in Friedreich's ataxia

Affiliations

¹ Departments of Pediatrics and Neurology, Children's Hospital of Philadelphia, Philadelphia, PA 19104-4318, USA; Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. Electronic address: lynchd@mail.med.upenn.edu.
² Departments of Pediatrics and Neurology, Children's Hospital of Philadelphia, Philadelphia, PA 19104-4318, USA.

Comment

David R Lynch et al. Lancet Neurol. 2016 Dec.

. 2016 Dec;15(13):1300-1301.

doi: 10.1016/S1474-4422(16)30281-2.

¹ Departments of Pediatrics and Neurology, Children's Hospital of Philadelphia, Philadelphia, PA 19104-4318, USA; Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, USA. Electronic address: lynchd@mail.med.upenn.edu.
² Departments of Pediatrics and Neurology, Children's Hospital of Philadelphia, Philadelphia, PA 19104-4318, USA.

No abstract available

Comment on

Progression characteristics of the European Friedreich's Ataxia Consortium for Translational Studies (EFACTS): a 2 year cohort study.
Reetz K, Dogan I, Hilgers RD, Giunti P, Mariotti C, Durr A, Boesch S, Klopstock T, de Rivera FJR, Schöls L, Klockgether T, Bürk K, Rai M, Pandolfo M, Schulz JB; EFACTS Study Group. Reetz K, et al. Lancet Neurol. 2016 Dec;15(13):1346-1354. doi: 10.1016/S1474-4422(16)30287-3. Lancet Neurol. 2016. PMID: 27839651 Clinical Trial.