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Comment

. 2016 Dec 17;388(10063):2964-2965.

doi: 10.1016/S0140-6736(16)32390-X. Epub 2016 Dec 7.

Dawn of a new therapeutic era for spinal muscular atrophy

Thomas H Gillingwater¹

Affiliations

Affiliation

¹ Euan MacDonald Centre for Motor Neurone Disease Research and Centre for Integrative Physiology, Edinburgh Medical School: Biomedical Sciences, University of Edinburgh, Edinburgh EH8 9AG, UK. Electronic address: T.Gillingwater@ed.ac.uk.

PMID: 27939062
DOI: 10.1016/S0140-6736(16)32390-X

Free article

Comment

Dawn of a new therapeutic era for spinal muscular atrophy

Thomas H Gillingwater. Lancet. 2016.

Free article

. 2016 Dec 17;388(10063):2964-2965.

doi: 10.1016/S0140-6736(16)32390-X. Epub 2016 Dec 7.

Author

Thomas H Gillingwater¹

Affiliation

¹ Euan MacDonald Centre for Motor Neurone Disease Research and Centre for Integrative Physiology, Edinburgh Medical School: Biomedical Sciences, University of Edinburgh, Edinburgh EH8 9AG, UK. Electronic address: T.Gillingwater@ed.ac.uk.

PMID: 27939062
DOI: 10.1016/S0140-6736(16)32390-X

No abstract available

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Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study.
Finkel RS, Chiriboga CA, Vajsar J, Day JW, Montes J, De Vivo DC, Yamashita M, Rigo F, Hung G, Schneider E, Norris DA, Xia S, Bennett CF, Bishop KM. Finkel RS, et al. Lancet. 2016 Dec 17;388(10063):3017-3026. doi: 10.1016/S0140-6736(16)31408-8. Epub 2016 Dec 7. Lancet. 2016. PMID: 27939059 Clinical Trial.

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