Dawn of a new therapeutic era for spinal muscular atrophy
- PMID: 27939062
- DOI: 10.1016/S0140-6736(16)32390-X
Dawn of a new therapeutic era for spinal muscular atrophy
Comment on
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Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study.Lancet. 2016 Dec 17;388(10063):3017-3026. doi: 10.1016/S0140-6736(16)31408-8. Epub 2016 Dec 7. Lancet. 2016. PMID: 27939059 Clinical Trial.
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