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. 2017 Jan 3;14(1):e1002191.
doi: 10.1371/journal.pmed.1002191. eCollection 2017 Jan.

What Is the Purpose of the Orphan Drug Act?

Matthew Herder  1
Affiliations

What Is the Purpose of the Orphan Drug Act?

Matthew Herder. PLoS Med. .

Abstract

Matthew Herder suggests it may be time to re-examine the purpose of the U.S. Orphan Drug Act.

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Conflict of interest statement

The author has declared that no competing interests exist.

References

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    1. Kesselheim A, Treasure CL, Joffe S. Biomarker-defined subsets of common diseases: policy and economic implications of Orphan Drug Act coverage. PLoS Med. 2016;14(1):e1002190 10.1371/journal.pmed.1002190 - DOI - PMC - PubMed
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