Efficient CRISPR/Cas9-based gene correction in induced pluripotent stem cells established from fibroblasts of patients with sickle cell disease

Affiliations

¹ Section of Gene Expression Regulation, Frontier Science Research Center, Kagoshima University, Kagoshima 890-8544, Japan.
² Division of Pediatric Dentistry, Department of Oral Health Sciences, Graduate School of Medical and Dental Sciences, Niigata University, Niigata 951-8514, Japan.
³ Department of Pediatric Dentistry, Graduate School of Medical and Dental Sciences, Kagoshima University, Kagoshima 890-8544, Japan.

Editorial

Masahiro Sato et al. Stem Cell Investig. 2016.

. 2016 Nov 14:3:78.

doi: 10.21037/sci.2016.11.05. eCollection 2016.

¹ Section of Gene Expression Regulation, Frontier Science Research Center, Kagoshima University, Kagoshima 890-8544, Japan.
² Division of Pediatric Dentistry, Department of Oral Health Sciences, Graduate School of Medical and Dental Sciences, Niigata University, Niigata 951-8514, Japan.
³ Department of Pediatric Dentistry, Graduate School of Medical and Dental Sciences, Kagoshima University, Kagoshima 890-8544, Japan.

No abstract available

Conflict of interest statement

The authors have no conflicts of interest to declare.

Naïve Induced Pluripotent Stem Cells Generated From β-Thalassemia Fibroblasts Allow Efficient Gene Correction With CRISPR/Cas9.
Yang Y, Zhang X, Yi L, Hou Z, Chen J, Kou X, Zhao Y, Wang H, Sun XF, Jiang C, Wang Y, Gao S. Yang Y, et al. Stem Cells Transl Med. 2016 Jan;5(1):8-19. doi: 10.5966/sctm.2015-0157. Epub 2015 Dec 16. Stem Cells Transl Med. 2016. PMID: 26676643 Free PMC article.

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