Patients with Gaucher type 1: Switching from imiglucerase to miglustat therapy
- PMID: 28111116
- DOI: 10.1016/j.bcmd.2017.01.007
Patients with Gaucher type 1: Switching from imiglucerase to miglustat therapy
Keywords: Gaucher; Imiglucerase; Substrate reduction therapy.
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