Comment
doi: 10.1126/scitranslmed.aam9864.
Rounding up sickle cells with gene therapy
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- PMID: 28298423
- DOI: 10.1126/scitranslmed.aam9864
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Comment
Rounding up sickle cells with gene therapy
Sci Transl Med.
.
Abstract
A report of a patient treated with ex vivo lentiviral gene transfer to hematopoietic stem cells shows the promise of gene therapy for sickle cell anemia.
Copyright © 2017, American Association for the Advancement of Science.
Comment on
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Gene Therapy in a Patient with Sickle Cell Disease.N Engl J Med. 2017 Mar 2;376(9):848-855. doi: 10.1056/NEJMoa1609677. N Engl J Med. 2017. PMID: 28249145
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