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. 2017 Apr;27(2):67-69.
doi: 10.1089/nat.2017.0665. Epub 2017 Feb 21.

FDA Approval of Nusinersen for Spinal Muscular Atrophy Makes 2016 the Year of Splice Modulating Oligonucleotides

Annemieke Aartsma-Rus  1
Affiliations

FDA Approval of Nusinersen for Spinal Muscular Atrophy Makes 2016 the Year of Splice Modulating Oligonucleotides

Annemieke Aartsma-Rus. Nucleic Acid Ther. 2017 Apr.
No abstract available

Keywords: antisense oligonucleotide; eteplirsen; nusinersen; spinal muscular atrophy; therapy.

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