Neurodegenerative disorders: Ataxin 2 reduction rescues motor defects

Comment

Sarah Crunkhorn. Nat Rev Drug Discov. 2017 Jun.

. 2017 Jun;16(6):384-385.

doi: 10.1038/nrd.2017.104. Epub 2017 May 19.

No abstract available

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Therapeutic reduction of ataxin-2 extends lifespan and reduces pathology in TDP-43 mice.
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Antisense oligonucleotide therapy for spinocerebellar ataxia type 2.
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