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Comment

. 2017 May 25;376(21):2093-4.

doi: 10.1056/NEJMc1704009.

Gene Therapy in a Patient with Sickle Cell Disease

Mohsin Badat^{1

2}, James Davies¹

Affiliations

PMID: 28541013
DOI: 10.1056/NEJMc1704009

Comment

Gene Therapy in a Patient with Sickle Cell Disease

Mohsin Badat et al. N Engl J Med. 2017.

. 2017 May 25;376(21):2093-4.

doi: 10.1056/NEJMc1704009.

Authors

Mohsin Badat^{1

2}, James Davies¹

Affiliations

¹ Medical Research Council Weatherall Institute of Molecular Medicine, Oxford, United Kingdom
² mohsin.badat@ndcls.ox.ac.uk

PMID: 28541013
DOI: 10.1056/NEJMc1704009

No abstract available

PubMed Disclaimer

Comment in

Gene Therapy in a Patient with Sickle Cell Disease.
Leboulch P, Cavazzana M. Leboulch P, et al. N Engl J Med. 2017 May 25;376(21):2094. doi: 10.1056/NEJMc1704009. N Engl J Med. 2017. PMID: 28538131 No abstract available.

Comment on

Gene Therapy in a Patient with Sickle Cell Disease.
Ribeil JA, Hacein-Bey-Abina S, Payen E, Magnani A, Semeraro M, Magrin E, Caccavelli L, Neven B, Bourget P, El Nemer W, Bartolucci P, Weber L, Puy H, Meritet JF, Grevent D, Beuzard Y, Chrétien S, Lefebvre T, Ross RW, Negre O, Veres G, Sandler L, Soni S, de Montalembert M, Blanche S, Leboulch P, Cavazzana M. Ribeil JA, et al. N Engl J Med. 2017 Mar 2;376(9):848-855. doi: 10.1056/NEJMoa1609677. N Engl J Med. 2017. PMID: 28249145

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