Cystic fibrosis transmembrane conductance-regulator modulators for children
- PMID: 28606619
- DOI: 10.1016/S2213-2600(17)30208-4
Cystic fibrosis transmembrane conductance-regulator modulators for children
Comment on
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Efficacy and safety of lumacaftor and ivacaftor in patients aged 6-11 years with cystic fibrosis homozygous for F508del-CFTR: a randomised, placebo-controlled phase 3 trial.Lancet Respir Med. 2017 Jul;5(7):557-567. doi: 10.1016/S2213-2600(17)30215-1. Epub 2017 Jun 9. Lancet Respir Med. 2017. PMID: 28606620 Clinical Trial.
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