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Comment
. 2017 Aug 2;25(8):1739-1740.
doi: 10.1016/j.ymthe.2017.06.001. Epub 2017 Jun 16.

Micromanaging Tolerance in Hemophilia A Gene Therapy

Jennielle Jobson  1 , Brian D Brown  2
Affiliations
Comment

Micromanaging Tolerance in Hemophilia A Gene Therapy

Jennielle Jobson et al. Mol Ther. .
No abstract available

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Comment on

  • A Novel Platform for Immune Tolerance Induction in Hemophilia A Mice.
    Merlin S, Cannizzo ES, Borroni E, Bruscaggin V, Schinco P, Tulalamba W, Chuah MK, Arruda VR, VandenDriessche T, Prat M, Valente G, Follenzi A. Merlin S, et al. Mol Ther. 2017 Aug 2;25(8):1815-1830. doi: 10.1016/j.ymthe.2017.04.029. Epub 2017 May 26. Mol Ther. 2017. PMID: 28552407 Free PMC article.

References

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    1. Oldenburg J., Lacroix-Desmazes S., Lillicrap D. Alloantibodies to therapeutic factor VIII in hemophilia A: the role of von Willebrand factor in regulating factor VIII immunogenicity. Haematologica. 2015;100:149–156. - PMC - PubMed

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