Skip to main page content
U.S. flag

An official website of the United States government

Dot gov

The .gov means it’s official.
Federal government websites often end in .gov or .mil. Before sharing sensitive information, make sure you’re on a federal government site.

Https

The site is secure.
The https:// ensures that you are connecting to the official website and that any information you provide is encrypted and transmitted securely.

Access keys NCBI Homepage MyNCBI Homepage Main Content Main Navigation
Review
. 2017 Aug 15;196(4):512-519.
doi: 10.1164/rccm.201703-0507WS.

Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary

Jonathan Finder  1 , Oscar Henry Mayer  2 , Daniel Sheehan  3 , Hemant Sawnani  4 , R Ted Abresch  5 , Joshua Benditt  6 , David J Birnkrant  7   8 , Tina Duong  9 , Erik Henricson  5 , Kathi Kinnett  10 , Craig M McDonald  5   11 , Anne M Connolly  12
Affiliations
Review

Pulmonary Endpoints in Duchenne Muscular Dystrophy. A Workshop Summary

Jonathan Finder et al. Am J Respir Crit Care Med. .

Abstract

Development of novel therapeutics for treatment of Duchenne muscular dystrophy (DMD) has led to clinical trials that include pulmonary endpoints that allow assessment of respiratory muscle status, especially in nonambulatory subjects. Parent Project Muscular Dystrophy (PPMD) convened a workshop in Bethesda, Maryland, on April 14 and 15, 2016, to summarize published respiratory data in DMD and give guidance to clinical researchers assessing the effect of interventions on pulmonary outcomes in DMD.

Keywords: Duchenne muscular dystrophy; outcome; respiratory failure.

PubMed Disclaimer

Comment in

MeSH terms