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Comment
. 2017 Dec;13(12):706-707.
doi: 10.1038/nrneurol.2017.152. Epub 2017 Oct 23.

Neurometabolic disease: Gene therapy success for cerebral adrenoleukodystrophy

Charlotte Ridler
Comment

Neurometabolic disease: Gene therapy success for cerebral adrenoleukodystrophy

Charlotte Ridler. Nat Rev Neurol. 2017 Dec.
No abstract available

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Comment on

  • Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy.
    Eichler F, Duncan C, Musolino PL, Orchard PJ, De Oliveira S, Thrasher AJ, Armant M, Dansereau C, Lund TC, Miller WP, Raymond GV, Sankar R, Shah AJ, Sevin C, Gaspar HB, Gissen P, Amartino H, Bratkovic D, Smith NJC, Paker AM, Shamir E, O'Meara T, Davidson D, Aubourg P, Williams DA. Eichler F, et al. N Engl J Med. 2017 Oct 26;377(17):1630-1638. doi: 10.1056/NEJMoa1700554. Epub 2017 Oct 4. N Engl J Med. 2017. PMID: 28976817 Free PMC article. Clinical Trial.

References

    1. N Engl J Med. 2017 Oct 26;377(17 ):1630-1638 - PubMed

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