Outrageous prices of orphan drugs: a call for collaboration

Collaborators, Affiliations

Second Workshop on Orphan Drugs participants:
Tiziano Barbui, Ariela Benigni, Enrico Costa, Erica Daina, Silvio Garattini, Donatella Gramaglia, Carla E M Hollak, Hanna Hyry, Helena Kaarinen, Christoph Licht, Lucio Luzzatto, Giampaolo Merlini, Rosario Notaro, Giuseppe Remuzzi, Franz Schaefer, Arrigo Schieppati, Steven Simoens

¹ Muhimbili University of Health and Allied Sciences, Dar-es-Salaam, Tanzania.
² Department of Medicine, University of Cambridge, Cambridge, UK.
³ Rare Disease Unit, Azienda Socio-Sanitaria Territoriale Papa Giovanni XXIII, Bergamo, Italy.
⁴ Pharmacy Service, Ospedale Policlinico "GB Rossi", Azienda Ospedaliera Universitaria Integrata, Verona, Italy.
⁵ KU Leuven Department of Pharmaceutical and Pharmacological Sciences, Leuven, Belgium.
⁶ Pediatric Nephrology Division, Heidelberg University Center for Pediatrics and Adolescent Medicine, Heidelberg, Germany.
⁷ Department of Molecular Medicine, University of Pavia, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy.
⁸ Genomics and Biomarkers Unit, National Institute for Health and Welfare, Helsinki, Finland.
⁹ IRCCS-Istituto di Ricerche Farmacologiche Mario Negri, Milano, Italy; IRCCS-Istituto di Ricerche Farmacologiche Mario Negri, Milano, Italy.
¹⁰ Department of Endocrinology and Metabolism, Academic Medical Center, Amsterdam, Netherlands.
¹¹ IRCCS-Istituto di Ricerche Farmacologiche Mario Negri, Bergamo, Italy; Unit of Nephrology and Dialysis, Azienda Socio-Sanitaria Territoriale Papa Giovanni XXIII, Bergamo, Italy; Department of Biomedical and Clinical Sciences, University of Milan, Milan, Italy. Electronic address: giuseppe.remuzzi@marionegri.it.

Lucio Luzzatto et al. Lancet. 2018.

. 2018 Sep 1;392(10149):791-794.

doi: 10.1016/S0140-6736(18)31069-9. Epub 2018 Jul 20.

Second Workshop on Orphan Drugs participants:
Tiziano Barbui, Ariela Benigni, Enrico Costa, Erica Daina, Silvio Garattini, Donatella Gramaglia, Carla E M Hollak, Hanna Hyry, Helena Kaarinen, Christoph Licht, Lucio Luzzatto, Giampaolo Merlini, Rosario Notaro, Giuseppe Remuzzi, Franz Schaefer, Arrigo Schieppati, Steven Simoens

¹ Muhimbili University of Health and Allied Sciences, Dar-es-Salaam, Tanzania.
² Department of Medicine, University of Cambridge, Cambridge, UK.
³ Rare Disease Unit, Azienda Socio-Sanitaria Territoriale Papa Giovanni XXIII, Bergamo, Italy.
⁴ Pharmacy Service, Ospedale Policlinico "GB Rossi", Azienda Ospedaliera Universitaria Integrata, Verona, Italy.
⁵ KU Leuven Department of Pharmaceutical and Pharmacological Sciences, Leuven, Belgium.
⁶ Pediatric Nephrology Division, Heidelberg University Center for Pediatrics and Adolescent Medicine, Heidelberg, Germany.
⁷ Department of Molecular Medicine, University of Pavia, Fondazione IRCCS Policlinico San Matteo, Pavia, Italy.
⁸ Genomics and Biomarkers Unit, National Institute for Health and Welfare, Helsinki, Finland.
⁹ IRCCS-Istituto di Ricerche Farmacologiche Mario Negri, Milano, Italy; IRCCS-Istituto di Ricerche Farmacologiche Mario Negri, Milano, Italy.
¹⁰ Department of Endocrinology and Metabolism, Academic Medical Center, Amsterdam, Netherlands.
¹¹ IRCCS-Istituto di Ricerche Farmacologiche Mario Negri, Bergamo, Italy; Unit of Nephrology and Dialysis, Azienda Socio-Sanitaria Territoriale Papa Giovanni XXIII, Bergamo, Italy; Department of Biomedical and Clinical Sciences, University of Milan, Milan, Italy. Electronic address: giuseppe.remuzzi@marionegri.it.

No abstract available

Comment in

Orphan drugs.
Cainelli F, Vento S. Cainelli F, et al. Lancet. 2019 Apr 20;393(10181):1594. doi: 10.1016/S0140-6736(19)30016-9. Lancet. 2019. PMID: 31007197 No abstract available.
Orphan drugs.
Messori A, Attanasio F, Trippoli S, Banfi R. Messori A, et al. Lancet. 2019 Apr 20;393(10181):1595. doi: 10.1016/S0140-6736(19)30015-7. Lancet. 2019. PMID: 31007198 No abstract available.
Orphan drugs.
Puig-Junoy J, Campillo-Artero C. Puig-Junoy J, et al. Lancet. 2019 Apr 20;393(10181):1595. doi: 10.1016/S0140-6736(19)30017-0. Lancet. 2019. PMID: 31007200 No abstract available.