TTR Gene Silencers for Hereditary ATTR Amyloidosis: More than ICER Recognized
- PMID: 30589634
- PMCID: PMC10398315
- DOI: 10.18553/jmcp.2019.25.1.015
TTR Gene Silencers for Hereditary ATTR Amyloidosis: More than ICER Recognized
Abstract
No funding support was received for the writing of this commentary. The author ser ves as a consultant for Akcea Therapeutics, Alnylam Phar maceuticals, Corino Therapeutics, Intellia Therapeutics, and Ionis Pharmaceuticals.
Conflict of interest statement
No funding support was received for the writing of this commentary. The author ser ves as a consultant for Akcea Therapeutics, Alnylam Phar maceuticals, Corino Therapeutics, Intellia Therapeutics, and Ionis Pharmaceuticals.
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References
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- Adams D, Gonzalez-Duarte A, O’Riordan WD, et al. . Patisiran, an RNAi therapeutic, for hereditary transthyretin amyloidosis. N Engl J Med. 2018;379(1):11-21. - PubMed
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- Benson MD, Waddington-Cruz M, Berk JL, et al. . Inotersen treatment for patients with hereditary transthyretin amyloidosis. N Engl J Med. 2018;379(1):22-31. - PubMed
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- Buxbaum JN. Oligonucleotide drugs for transthyretin amyloidosis. N Engl J Med. 2018;379(1):82-85. - PubMed
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