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. 2019 Jul;18(7):479-480.
doi: 10.1038/nrd.2018.128.

Defining orphan conditions in the context of the European orphan regulation: challenges and evolution

Daniel J O'Connor  1 , Maria E Sheean  2   3 , Matthias P Hofer  2 , Stelios Tsigkos  2 , Segundo Mariz  2 , Laura Fregonese  2 , Kristina Larsson  2 , Virginie Hivert  4 , Kerstin Westermark  5 , Frauke Naumann-Winter  6 , Violeta Stoyanova-Beninska  7 , Ingeborg Barišić  8 , Giuseppe Capovilla  9 , Armando Magrelli  10 , Bruno Sepodes  11
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Defining orphan conditions in the context of the European orphan regulation: challenges and evolution

Daniel J O'Connor et al. Nat Rev Drug Discov. 2019 Jul.
No abstract available

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