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Clinical Trial
. 2019 Nov;90(11):1291-1293.
doi: 10.1136/jnnp-2018-320283. Epub 2019 Apr 4.

Long-term follow-up in an open-label trial of triheptanoin in GLUT1 deficiency syndrome: a sustained dramatic effect

Elodie Hainque  1   2 , Domitille Gras  3 , Aurélie Meneret  1   2 , Mariana Atencio  2 , Marie-Pierre Luton  2 , Magali Barbier  2 , Mohamed Doulazmi  4 , Florence Habarou  5 , Chris Ottolenghi  5 , Emmanuel Roze  1   2   6 , Fanny Mochel  7   6   8
Affiliations
Clinical Trial

Long-term follow-up in an open-label trial of triheptanoin in GLUT1 deficiency syndrome: a sustained dramatic effect

Elodie Hainque et al. J Neurol Neurosurg Psychiatry. 2019 Nov.
No abstract available

Keywords: GLUT1 deficiency syndrome; movement disorders; triheptanoin.

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Conflict of interest statement

Competing interests: FM holds a patent on the use of triheptanoin in GLUT1-DS (WO2014093901).

Figures

Figure 1
Figure 1
(A) Flow chart. (B) Normalised number of paroxysmal events in patients with glucose transporter type 1 deficiency syndrome (GLUT1-DS) during the different phases of the study. Total and motor numbers of paroxysmal events are expressed in mean per month. Error bars represent SEM. *P<0.05 (Dunn’s tests). m, number of months; n, number of patients.
See this image and copyright information in PMC

References

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MeSH terms

Supplementary concepts