Nusinersen for spinal muscular atrophy: Not just for babies?
- PMID: 31019098
- DOI: 10.1212/WNL.0000000000007559
Nusinersen for spinal muscular atrophy: Not just for babies?
Comment on
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Nusinersen in later-onset spinal muscular atrophy: Long-term results from the phase 1/2 studies.Neurology. 2019 May 21;92(21):e2492-e2506. doi: 10.1212/WNL.0000000000007527. Epub 2019 Apr 24. Neurology. 2019. PMID: 31019106 Free PMC article. Clinical Trial.
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