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Editorial
. 2019 Aug 8;381(6):579-580.
doi: 10.1056/NEJMe1906771. Epub 2019 Jun 14.

A Targeted Agent for Sickle Cell Disease - Changing the Protein but Not the Gene

Alexis Thompson  1
Affiliations
Editorial

A Targeted Agent for Sickle Cell Disease - Changing the Protein but Not the Gene

Alexis Thompson. N Engl J Med. .
No abstract available

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  • A Phase 3 Randomized Trial of Voxelotor in Sickle Cell Disease.
    Vichinsky E, Hoppe CC, Ataga KI, Ware RE, Nduba V, El-Beshlawy A, Hassab H, Achebe MM, Alkindi S, Brown RC, Diuguid DL, Telfer P, Tsitsikas DA, Elghandour A, Gordeuk VR, Kanter J, Abboud MR, Lehrer-Graiwer J, Tonda M, Intondi A, Tong B, Howard J; HOPE Trial Investigators. Vichinsky E, et al. N Engl J Med. 2019 Aug 8;381(6):509-519. doi: 10.1056/NEJMoa1903212. Epub 2019 Jun 14. N Engl J Med. 2019. PMID: 31199090 Clinical Trial.

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