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Comment
. 2020 Mar;62(3):267.
doi: 10.1111/dmcn.14447. Epub 2019 Dec 26.

Current and future treatments of spinal muscular atrophy

Martin Smith  1
Affiliations
Free article
Comment

Current and future treatments of spinal muscular atrophy

Martin Smith. Dev Med Child Neurol. 2020 Mar.
Free article
No abstract available

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References

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    1. Aragon-Gawinska K, Daron A, Ulinici A, et al. Sitting in patients with spinal muscular atrophy type 1 treated with nusinersen. Dev Med Child Neurol 2020; 62: 310-4.
    1. Schorling DC, Pechmann A, Kirschner J. Advances in treatment of spinal muscular atrophy - new phenotypes, new challenges, new implications for care. J Neuromuscul Dis 2020; 62: 310-4.
    1. Boardman FK, Young PJ, Griffiths FE. Newborn screening for spinal muscular atrophy: The views of affected families and adults. Am J Med Genet 2017; 173A: 1546-61.
    1. Boardman FK, Sadler C, Young PJ. Newborn genetic screening for spinal muscular atrophy in the UK: The views of the general population. Mol Genet Genomic Med 2018; 6: 99-108.

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