Editorial
doi: 10.3949/ccjm.87a.19124.
Epub 2020 Jan 2.
Gene therapy in sickle cell disease: Possible utility and impact
Affiliations
- PMID: 31990652
- DOI: 10.3949/ccjm.87a.19124
Item in Clipboard
Editorial
Gene therapy in sickle cell disease: Possible utility and impact
Cleve Clin J Med.
2020 Jan.
Free article
No abstract available
Similar articles
-
A pause in gene therapy: Reflecting on the unique challenges of sickle cell disease.Mol Ther. 2021 Apr 7;29(4):1355-1356. doi: 10.1016/j.ymthe.2021.03.010. Epub 2021 Mar 19. Mol Ther. 2021. PMID: 33743192 Free PMC article. No abstract available.
-
Gene therapy is facing its biggest challenge yet.Nature. 2019 Dec;576(7785):22-25. doi: 10.1038/d41586-019-03698-8. Nature. 2019. PMID: 31797915 No abstract available.
-
Promise of gene therapy to treat sickle cell disease.Expert Opin Biol Ther. 2018 Nov;18(11):1123-1136. doi: 10.1080/14712598.2018.1536119. Epub 2018 Oct 19. Expert Opin Biol Ther. 2018. PMID: 30324810 Review.
-
Gene therapy renews hope to lower the global rural sickle cell disease burden.Rural Remote Health. 2017 Jul-Sep;17(3):4291. doi: 10.22605/RRH4291. Epub 2017 Sep 7. Rural Remote Health. 2017. PMID: 28877587 No abstract available.
-
Emerging Genetic Therapy for Sickle Cell Disease.Annu Rev Med. 2019 Jan 27;70:257-271. doi: 10.1146/annurev-med-041817-125507. Epub 2018 Oct 24. Annu Rev Med. 2019. PMID: 30355263 Review.
Cited by
-
Curative vs targeted therapy for SCD: does it make more sense to address the root cause than target downstream events?Blood Adv. 2020 Jul 28;4(14):3457-3465. doi: 10.1182/bloodadvances.2020001469. Blood Adv. 2020. PMID: 32722787 Free PMC article.
-
Evidence-Based Minireview: In young children with severe sickle cell disease, do the benefits of HLA-identical sibling donor HCT outweigh the risks?Hematology Am Soc Hematol Educ Program. 2021 Dec 10;2021(1):190-195. doi: 10.1182/hematology.2021000322. Hematology Am Soc Hematol Educ Program. 2021. PMID: 34889371 Free PMC article. Review.
Publication types
MeSH terms
LinkOut - more resources
Full Text Sources
Medical
