Broader Implications of Progressive Liver Dysfunction and Lethal Sepsis in Two Boys following Systemic High-Dose AAV

Affiliations

¹ Biomedical Graduate Studies, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
² School of Arts and Sciences, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
³ Department of Ophthalmology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
⁴ Department of Surgery, Perelman School of Medicine, University of Pennsylvania and Corporal Michael Crescenz Veterans Affairs Medical Center, Philadelphia, PA, 19104, USA. Electronic address: hstedman@pennmedicine.upenn.edu.

Editorial

Leon Morales et al. Mol Ther. 2020.

. 2020 Aug 5;28(8):1753-1755.

doi: 10.1016/j.ymthe.2020.07.009. Epub 2020 Jul 16.

¹ Biomedical Graduate Studies, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
² School of Arts and Sciences, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
³ Department of Ophthalmology, Perelman School of Medicine, University of Pennsylvania, Philadelphia, PA, 19104, USA.
⁴ Department of Surgery, Perelman School of Medicine, University of Pennsylvania and Corporal Michael Crescenz Veterans Affairs Medical Center, Philadelphia, PA, 19104, USA. Electronic address: hstedman@pennmedicine.upenn.edu.

No abstract available

References

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