Re: "Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy" by Wilson and Flotte

Affiliations

¹ University of California at Los Angeles School of Medicine, Los Angeles, California, USA.
² National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, Maryland, USA.
³ Klinikum der Universität München, Munich, Germany.
⁴ Hospital for Sick Children, Toronto, Ontario, Canada.
⁵ Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA.
⁶ Institute of Myology, Pitié-Salpêtrière Hospital, Paris, France.

Comment

Perry B Shieh et al. Hum Gene Ther. 2020 Aug.

. 2020 Aug;31(15-16):787.

doi: 10.1089/hum.2020.217.

¹ University of California at Los Angeles School of Medicine, Los Angeles, California, USA.
² National Institute of Neurological Disorders and Stroke, National Institutes of Health, Bethesda, Maryland, USA.
³ Klinikum der Universität München, Munich, Germany.
⁴ Hospital for Sick Children, Toronto, Ontario, Canada.
⁵ Ann and Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, USA.
⁶ Institute of Myology, Pitié-Salpêtrière Hospital, Paris, France.

No abstract available

Comment on

Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy.
Wilson JM, Flotte TR. Wilson JM, et al. Hum Gene Ther. 2020 Jul;31(13-14):695-696. doi: 10.1089/hum.2020.182. Epub 2020 Jul 1. Hum Gene Ther. 2020. PMID: 32605399 No abstract available.

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