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Case Reports
. 2020 Dec;51(6):450-452.
doi: 10.1055/s-0040-1715486. Epub 2020 Sep 6.

Sandhoff Disease: Improvement of Gait by Acetyl-DL-Leucine: A Case Report

Tatiana Bremova-Ertl  1   2 , Frances Platt  3 , Michael Strupp  1
Affiliations
Case Reports

Sandhoff Disease: Improvement of Gait by Acetyl-DL-Leucine: A Case Report

Tatiana Bremova-Ertl et al. Neuropediatrics. 2020 Dec.
No abstract available

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Conflict of interest statement

T.B.-E. received honoraria for lecturing from Actelion and Sanofi-Genzyme.F.P. is a Royal Society Wolfson Research Merit Award holder and a Wellcome Trust Investigator in Science. F.P. is an academic co-founder of IntraBio and a share holder in IntraBio.M.S. is Joint Chief Editor of the Journal of Neurology, Editor in Chief of Frontiers of Neuro-otology and Section Editor of F1000. He has received speaker's honoraria from Abbott, Actelion, Auris Medical, Biogen, Eisai, Grünenthal, GSK, Henning Pharma, Interacoustics, MSD, Otometrics, Pierre-Fabre, TEVA, and UCB. He is a shareholder of IntraBio. He is the distributor of M glasses. He acts as a consultant for Abbott, Actelion, AurisMedical, Heel, IntraBio, and Sensorion.